What questions do you have about gene therapy?

We want your input!

The Patient Advocacy & Engagement team at Astellas Gene Therapies is dedicated to integrating the perspective of patients and their families into our work. By doing so, we believe that we can more effectively deliver development programs, education, resources and support to the communities.

Rather than developing materials that we think would be helpful, we want to hear from you! We truly value your thoughts and opinions and we welcome you to ask as many questions as you might have related to gene therapy. All of your questions will inspire the content we include in our educational materials.

Please note: All of your answers will be anonymous. We ask that you do not provide any personally identifying health information.

We value your input. Thank you in advance for your time!

Sincerely,

The Patient Advocacy & Engagement Team

Question Title

* 1. I am a...

Person living with a rare condition

Family member of a person living with a rare condition

Other (please specify)

Question Title

* 2. Which rare condition do you or your family member have?

X-Linked Myotubular Myopathy

Pompe Disease

Duchenne Muscular Dystrophy

Myotonic Dystrophy Type 1

None

Other (please specify)

Question Title

* 3. What questions do you have about gene therapy?

Please list as many as you would like within the box below.

Example questions:
- How does gene therapy work?
- How do you administer gene therapy to a person?
- What are the different types of gene therapy?

Question Title

* 1. I am a...

Question Title

* 2. Which rare condition do you or your family member have?

Question Title

* 3. What questions do you have about gene therapy? Please list as many as you would like within the box below.Example questions:- How does gene therapy work?- How do you administer gene therapy to a person?- What are the different types of gene therapy?

* 3. What questions do you have about gene therapy?

Please list as many as you would like within the box below.

Example questions:
- How does gene therapy work?
- How do you administer gene therapy to a person?
- What are the different types of gene therapy?