Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance Orphazyme is investigating is called arimoclomol citrate, which is administered orally via hard capsules three times a day (morning, noon and evening). As with many active substances, the taste of arimoclomol citrate can be perceived as bitter. Capsules may be administered in two ways:

•       Swallowed whole with a suitable amount of liquid
•       Capsules may be opened and the powder dispersed into a liquid or soft food

Regulatory guidelines require that Orphazyme demonstrates the appropriate compatibility of arimoclomol in various liquids and soft foods. Orphazyme would like your opinion on which liquids and soft foods you may prefer for the administration of oral medicinal products, to ensure that information provided to regulatory authorities is representative of what NPC patients and families are most likely to use. Thank you for taking a few minutes to share your opinion.

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* 2. Are you a person living with NPC or a caregiver of someone living with NPC?

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* 3. If you are a caregiver, are you responding on behalf of a child or an adult living with NPC?

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* 4. If you were to take an oral medication mixed with a soft food or liquid -- or administer an oral medication, if you are a caregiver -- which foods or liquids would you prefer to use? Please rank the following options from 1 (best) to 6 (less preferred):

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* 5. Are there other soft foods or liquids that you prefer to use when administering or taking an oral medication?

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