Purpose:
We’re seeking Wilson disease (WD) patients and caregivers to share their real-world experiences via video for our upcoming Externally-Led Patient-Focused Drug Development (EL-PFDD) meeting. These videos will help educate FDA regulators and other stakeholders—such as medical product developers, clinicians, and researchers—about the symptoms that matter most, how WD impacts daily life, and patient experiences with current treatments. Your voice can help shape future therapies, guide oversight during drug development, and inform FDA decision-making.
We’re seeking Wilson disease (WD) patients and caregivers to share their real-world experiences via video for our upcoming Externally-Led Patient-Focused Drug Development (EL-PFDD) meeting. These videos will help educate FDA regulators and other stakeholders—such as medical product developers, clinicians, and researchers—about the symptoms that matter most, how WD impacts daily life, and patient experiences with current treatments. Your voice can help shape future therapies, guide oversight during drug development, and inform FDA decision-making.