Skip to content
CRA's Project LEOPARD Survey
*
1.
Please provide us with your name, company, job title, and email.
(Required.)
Name
Company & Job Title
Email Address
2.
How do you prefer to receive updates and thought pieces on rare disease?
Articles
Infographics
Podcasts & videos
Webinars & roundtables
Other (please specify)
3.
What rare disease topics do you want to hear more about?
Trends in Orphan Medicinal Product (OMP) policy/assessment
How to find rare disease patients
Optimization of rare disease care pathways
Justifying OMP value with evidence
Other (please specify)
4.
For established/addressed rare diseases with product(s) indicated, please select the top three future trends you consider most important for rare disease companies
Higher bar for evidence
Need for innovative forms of engagement to differentiate
Increasing price pressure
Subject to restriction or tendering
Commercial opportunity trade-offs given market maturity
LoE exacerbating competition
Proactive targeting of niche/subpopulation
Other (please specify)
Does not apply
5.
For unaddressed rare diseases with high unmet needs, please select the top three future trends you consider most important for rare disease companies
Lower evidence expectations for first to market
Alternative access approaches to alleviate uncertainty
Increased payer scrutiny of “rare” or “orphan”
Competitive role for patient finding to accelerate access & uptake
Increasing RD affordability concerns
Need to establish patient support “beyond the pill”
Other (please specify)
Does not apply
6.
For rare subcategories/segments of non-rare conditions, please select the top three future trends you consider most important for rare disease companies
Need to show incremental value in rare sub-category
Dissociating messaging from parent non-rare disease
Strict management approaches to prevent spillover
Reliable diagnosis and precision medicine expectations
Development of distinct care pathways
Other (please specify)
Does not apply
7.
Of the rare disease critical success factors, which (up to three) would you like to hear more about?
Identifying unmet need
Precision medicine
Evidence generation
Market shaping
Stakeholder engagement
Go-to-market strategy
*
8.
Would you be open to a follow up relating to Project Leopard? If yes, we will use the email address provided above. If you prefer a different email address, please provide below.
(Required.)
Yes
No
Best email address for contact
Current Progress,
0 of 8 answered
