About this survey

Thank you so much for your time! You have been invited to take this survey because you may be a person with PK deficiency or you may be a parent or guardian (caregiver) to a child with PK deficiency.

If you have PK deficiency, we would like you to answer based on your own experience as a person living with PK deficiency. If you are a parent of a child with PK deficiency, please answer the survey based on your child’s experiences. And if you are both a person with PK deficiency and a parent to a child with PK deficiency, please answer the survey based on your own experience as a person living with PK deficiency.

This survey was created by Agios Pharmaceuticals, a commercial, for-profit company committed to transforming the lives of people with PK deficiency by investigating new therapies for the disease. We deeply appreciate you taking the time to tell us about your experiences with PK deficiency. By sharing your thoughts today, you can help improve our understanding and research for the future.

Cambridge BioMarketing is conducting this survey on behalf of Agios. By answering the questions below, you are agreeing to allow us to share your responses with Agios. All of the information you provide will be anonymous (it will not identify you in any way) unless you provide your name at the end of this survey. Your individual information will not be shared outside of Cambridge BioMarketing and Agios. If we do share your responses to the survey, they will always be combined with information from other people who have responded to this survey and will not identify you in any way.

The information gathered through this survey will help Cambridge BioMarketing and Agios better understand PK deficiency and the impact it has on the lives of patients and their parents.

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